There is currently no cure for Alpha-Mannosidosis, and treatment is often limited to addressing or controlling symptoms.1
There is currently no cure for Alpha-Mannosidosis, and treatment is often limited to addressing or controlling symptoms.1
A proactive approach is adopted to prevent any emerging complications, and a thorough clinical assessment is carried out at the time of initial diagnosis.1
Rationale for treatment: with this condition, all cells are without α-mannosidase activity. The rationale for HSCT in this setting is that enzyme-producing donor cells repopulate the host tissues and transfer enzyme to nearby enzyme-deficient host cells.